The company said participants will receive a GLP-1 washout before receiving RJVA-001 delivered via endoscopic ...
In a worldwide first, a one-and-done gene therapy has been approved to treat a form of hereditary deafness. Many of the ...
Add Yahoo as a preferred source to see more of our stories on Google. Wilsey, a Mashpee Wampanoag Tribe member, was diagnosed with sickle cell disease at birth. He started gene therapy on May 16, ...
Authorization advances Fractyl Health to a dual clinical-stage company, with Revita® in pivotal development for post-GLP-1 weight maintenance and ...
The search for gene therapies to treat rheumatoid arthritis (RA) has moved in fits and starts over the past two decades, with trials starting and stopping, and their focus shifting to osteoarthritis ...
Tinkering with the genetic code of a living human is risky. The post Gene Therapy Causes Patient to Grow Alarming Tumor ...
The first peer-reviewed journal in the field of human gene therapy, providing all-inclusive coverage of the research, methods, and clinical developments that are driving today's explosion of gene ...
A planned first-in-human trial aims to treat GM1 gangliosidosis in utero, possibly laying the foundation for prenatal gene ...
Researchers in the WashU Medicine Department of Ophthalmology & Visual Sciences have discovered key neuroprotective genes ...
Scientists from Spirovant Sciences describe SP-101, a novel adeno-associated virus (AAV) gene therapy for the treatment of cystic fibrosis (CF) in the peer-reviewed journal Human Gene Therapy. They ...
On April 14, 2026, the United States Food and Drug Administration (“FDA”) issued a draft guidance for sponsors seeking approval of human ...