An experimental gene therapy for a rare form of genetic deafness has successfully restored hearing in children and adults, ...
A first-of-its-kind gene therapy that can restore hearing in children born deaf has just cleared its final hurdle—and, in a ...
Travis used to sleep through everything. Then his mother laughed in the car and woke him up, the first time he had ever heard ...
Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...
Cell and gene therapies are currently niche products, even within specialty pharmacy, drugs that, by most definitions, are ...
When Santa Claus brought 10-year-old Kathy High a junior chemistry set for Christmas more than 60 years ago, he never could’ve imagined what an incredible gift he was giving her. And ...
Innovations in pharmacy are already delivering results, but there is still work to do to evolve the ecosystem, said Ryan ...
Three Philadelphia scientists won a $3 million Breakthrough Prize for developing the first FDA-approved gene therapy for a genetic disease, prize sponsors announced Saturday. Their work created a ...